23rd May 2025 Plain language summary: how patients reported their experiences with avalglucosidase alfa and alglucosidase alfa in the COMET trial
14th Feb 2024 Long-term benefits of enzyme replacement therapy in children and teenagers with Gaucher disease type 3- a plain language summary
25th Nov 2022 Plain language summary of a study looking at the age at diagnosis and time to start of treatment in individuals with mucopolysaccharidosis type I (MPS I)
