A plain language summary looking at how the effects of gene therapy based on adeno-associated virus last

This Plain Language Summary of Publication article (PLSP) from Future Rare Diseases summarises several scientific articles and discusses how long the effects of one type of gene therapy (based on adeno-associated virus) last. Gene therapy is a technique that uses a gene(s) to treat, prevent or cure a disease or medical disorder.

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This PLSP is based on an article called ‘Durability of transgene expression after rAAV gene therapy’ and was published in Molecular therapy. 

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• gene therapy
• lay summary
• plain language summary
• rare disease

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