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Cell and Gene Therapy

15th Aug 2025

Early research on AAV5-hRKp.RPGR treatment for X-linked vision disorder linked to the RPGR gene: a plain language summary

his is a summary of a review article about gene therapy. Review articles summarize many previously published scientific articles. The review was about how a common virus could change how one type of gene therapy works. It also discussed the importance of antibody testing for people who may receive gene therapy. The original review was published in Molecular Therapy in 2023

22nd Jan 2024

Cell and Gene Therapy

Early research on AAV5-hRKp.RPGR treatment for X-linked vision disorder linked to the RPGR gene: a plain language summary

A plain language summary of the challenges and solutions for people with antibodies against AAV-based gene therapy